Pipeline

Retrophin is focused on finding and developing treatments for conditions with specific characteristics, including those: (1) that are debilitating and often lethal, with a high cost to the system and patient, and where patients experience a low quality of life; (2) that are well understood, with scientific consensus regarding the cause; and (3) for which we believe the development timeline will be rapid.

Product/Program Pre-Clinical Phase I Phase II Phase III Market
Chenodal:
Gallstones
Cerebrotendinous xanthomatosis  
Vecamyl:
Hypertension
Rage Disorders        
Syntocinon Nasal Spray:
Lactation  
Schizophrenia    
Autism    
Sparsentan:
Focal Segmental Glomerulosclerosis  
RE-024:
Pantothenate Kinase
Associated Neurodegeneration
 
RE-034:
Infantile Spasms
Nephrotic Syndrome
RE-001:
Duchenne Muscular Dystrophy