NGLY Collaboration & Discovery Efforts
We are collaborating with the National Center for Advancing Translational Sciences (NCATS) Therapeutics for Rare and Neglected Diseases (TRND) Biology Laboratory, and patient advocacy foundation NGLY1.org on a research plan to develop different assays for small molecule high-throughput screening. This is being done in both an effort to better understand the biology of the disease, as well as identify potential small molecules to be developed as a therapeutic for patients suffering from NGLY deficiency.
Learn more about this partnership.
We seek opportunities to acquire late-stage clinical assets or commercial-ready medicines that fit within our strategy of addressing rare diseases with significant unmet medical needs.
We invite potential partners who share our goals to contact us at firstname.lastname@example.org.