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Creating Hope

by identifying, developing and delivering life-changing therapies to people living with rare diseases.

Creating Hope

by identifying, developing and delivering life-changing therapies to people living with rare diseases.

Creating Hope

by identifying, developing and delivering life-changing therapies to people living with rare diseases.

We are a biopharmaceutical company focused on developing our pipeline featuring sparsentan, a product candidate in late-stage development for focal segmental glomerulosclerosis (FSGS) and IgA nephropathy (IgAN), rare disorders characterized by progressive scarring of the kidney often leading to end-stage renal disease. Research in additional rare diseases is also underway, including partnerships with leaders in patient advocacy and government research to identify potential therapeutics for NGLY1 deficiency and Alagille syndrome, conditions with no approved treatment options.

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Therapeutic Focus

Retrophin is a biopharmaceutical company focused on discovering, developing and marketing innovative therapies for debilitating and often life-threatening diseases.  We are dedicated to working in areas in which the biopharmaceutical industry has, to date, had limited interest or effectiveness.  We maintain a focus on patients, working with doctors and patient advocacy groups and seeking to understand their distinct needs.